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Ultragenyx Presents

GSDIa From Today to Tomorrow:
Educational Satellite Symposium at ACMG 2025
When
Where
March 19th, 2025
8am - 9:30am
JW Marriott LA:
Gold Ballroom 4
Navigating Today's Challenges & Looking Ahead into the Gene Therapy Pipeline
Learning Objectives
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Review unmet needs and challenges that persist in GSDIa
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Review gene therapy approaches under development for GSDIa
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Gene therapy: Practical considerations for implementation at clinical centers
Register now to attend
The Speakers
Learn about our industry professionals

Dr. Areeg El-Gharbawy
Associate Professor of Pediatrics
Division of Medical Genetics & Genomics, Dept of Pediatrics
Duke University Medical Center

Dr. Carlos Prada
Professor of Pediatrics
Division of Genetics, Genomics, & Metabolism
Lurie Children’s Hospital, Northwestern University

Dr. Steven Pipe
Professor of Pediatrics & Pathology
Department of Pathology
C.S.Mott Children’s Hospital, University of Michigan
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